Twitter | Search | |
Search Refresh
UCSF Benioff SF Apr 17
Exciting news! Our doctors have been working with researchers at on a new gene therapy to cure babies born without immune systems. The first 10 children in the study have experienced life-changing results.
Reply Retweet Like
Lara Yuan Apr 18
Truly some exciting progress for the community and for , but please stop reporting this story with reference to the vector as , it is not doing anyone any favors and so easily leads to misinformation. I'm looking at you, .
Reply Retweet Like
World News Network Apr 17
Reply Retweet Like
Larry Ward, MD Apr 17
This would be amazing news! Curing immunodeficiencies. Wow. We definitely are living in interesting times.
Reply Retweet Like
St. Jude Research Apr 18
Gene therapy first: Newborns with SCID-X1, also known as “bubble boy” disease, have fully functional immune system for the first time with no apparent side effects.
Reply Retweet Like
St. Jude Research Apr 17
Learn about a gene therapy developed at St. Jude that results in a complete cure of SCID-X1.
Reply Retweet Like
Aria Marketing 14h
Scientists think they’ve found a way to better treat, and potentially cure . Learn more from :
Reply Retweet Like
Evangelia Loizou Apr 22
After decades of work and horrible off-target effects this is such great news for patients with SCID-X1 disease without the option for a matched donor! What's next for lentiviral gene therapy? -X1
Reply Retweet Like
Prof. Bobby Gaspar Apr 22
Wonderful and moving story! Congratulations !!
Reply Retweet Like
St. Jude Research Apr 19
Gene therapy pioneered at St. Jude cures infants with “bubble boy” disease. Nature:
Reply Retweet Like
JLittles Apr 18
the vector is not but utilitizes a component of it to transfer the genome 🧬 this is not the virus. Thanks for sharing this story as children are treated for this disease hoping for a cure from .
Reply Retweet Like
Linen Press Apr 22
writes an ode to the in memoir A Roll of the Dice which we are publishing today! As her 1st child was born with so began a journey from India to London for rare treatment. Check it out & thanks for all the vital work you do!
Reply Retweet Like
UCSFChildrensOakland Apr 18
New gene therapy from results in complete cure of "bubble boy" immune disease SCID-X1.
Reply Retweet Like
IDF Apr 19
Researchers at revealed promising study results related to gene therapy treatment options for X-linked Severe Combined Immunodeficiency (), one of the most severe forms of primary immunodeficiency diseases (PI). Read more on our blog:
Reply Retweet Like
𝙺𝚛𝚒𝚜𝚝𝚘𝚏𝚎𝚛 𝙴𝚒𝚜𝚎𝚗𝚕𝚊 Apr 17
From : Doctors develop 'cure' for babies with 'bubble boy' disease
Reply Retweet Like
ResearchAmerica Apr 16
1) Severe combined immunodeficiency is a fatal immune disorder that causes death before an infant's second birthday. Now, research-based newborn screening allows babies to be diagnosed with at birth, and treated with a bone marrow transplant to restore immune function
Reply Retweet Like
St. Jude Research Apr 17
You’ve heard of “bubble boy” disease. Learn about how is diagnosed, treated and the research behind improving the lives of these patients. .
Reply Retweet Like
Genome Medical, Inc. Apr 18
Additional work showing how can cure certain types of genetic disorders, in this case . Very exciting work for individuals with genetic disorders of the immune system.
Reply Retweet Like
Tom Folan Apr 18
In a world which can increasingly seem like it is tethered to a one way ticket to hell in a handbasket, we need more news like this: “An experimental gene therapy has cured eight infants with the so-called Bubble Boy Disease...”
Reply Retweet Like
Irene Tien MD FACEP Apr 21
Sometimes real life sounds like sci-fi! This is an amazing advancement for children with .
Reply Retweet Like