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Shelley Simmonds 23h
Exactly 5 years ago I cried tears of sorrow - I’d been told my baby boy would never be able to walk. Tonight I sat here and cried tears of joy as I watched my now nearly 6 year old take some first little unaided steps. Sometimes timing is so powerful. SURREAL.
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Gary Fegan 2h
Cardiologist appointment tomorrow. Like the ghost of Christmas yet to come is to scrooge, of all the appointments we go to, this is the one I fear the most.
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UT Southwestern News Feb 19
The right treatment can extend the life of those with muscular dystrophy or . cardiologist Pradeep Mammen, M.D., explains how.
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Harrison's Fund 13h
Is your energy bill higher than you'd like? Check out ethical energy suppliers and see if you could save. Quote HF1005 and they donate to us when you switch! If everyone following us did that we could fund amazing work for a cure for .
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Alex's Wish Feb 17
Every week in the UK two people are diagnosed with - the most common fatal genetic disorder diagnosed in childhood . Find out more here
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Hemi Malkki 6h
1-year evaluation of AAV-CRISPR genome editing in a mouse model for muscular dystrophy shows sustained dystrophin protein restoration - but also raises questions regarding unintended genome editing outcomes and host response
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Action Duchenne 3h
Exciting news! International best seller is auctioning a NAME in one of his future Roy Grace books for us! The reserve is just £750! If you are interested, all bids should be emailed to: nameinabook@hotmail.com A huge THANK YOU to Peter! 😃
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Shelley Simmonds Feb 18
Tonight while cruising the sofa, the little boy fell down 3 times. He’s never fallen down that many times in a row before. Mind now in overdrive.
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Charley's Fund Feb 14
It’s Valentine’s Day & we’re halfway through “We ❤ Our Supporters” month. Today’s honoree is Lisa Baldwin, faculty advisor to the club at Monument Mountain Regional High School. Under Lisa’s advisement, the group has raised over $20K for the fight against
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John Devlin 5h
I hate giving my son steroids but reluctantly do so. The boys have enough to deal with without increased emotional upheaval because of steroids' physical side effects marking them out from their peers. This sounds really promising
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Endpoints News 7h
Applying to , Duke researchers spotlight 1-year mouse data in Sarepta-sponsored study
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Duchenne Awareness UK Feb 19
It’s featured family day! Tonight mum Alexzandra talks to us about her son Spencer, who was diagnosed 6 months ago with
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dr.Bernard Feb 12
Replying to @MarleenStelling
Stay strong 💪 I raised 3 kids youngest got
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PTC Therapeutics 8h
Our 2019 PRIORITY Program seeks to fund innovative research to improve and increase screening methods, reducing the average age of diagnosis in infants with muscular dystrophy.
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Harrison's Fund 7h
Great morning at . We watched the team train, join them on the pitch afterwards &even have lunch! Danny Ward, Head Coach is running the for us next month. Support Danny …/danny-ward-surrey…
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Duchenne Awareness UK Feb 14
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Australian Disability Limited Feb 18
Researchers have shown that a single systemic treatment using CRISPR genome editing technology can safely and stably correct a genetic disease -- (DMD) -- for more than a year in mice,...
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Shelley Simmonds Feb 14
. Members Meeting today and Parent Project’s International Conference this weekend in Rome. My first time at both of these - looking forward to seeing some of the best people who do so much for . cc.
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Charley's Fund Feb 13
Years ago Rachel and Hope Suttin of Waban, MA wandered into the store and dropped a pretty penny. That was only the beginning of their contribution to the fight against . We’re grateful and honored to have the Suttin family on our side!
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Terry's Foundation for Muscular Dystrophy Feb 14
has announced that the FDA has accepted its New Drug Application (NDA) seeking accelerated approval for golodirsen (SRP-4053). Check out the full press release below:
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